Endosomal Escape Vehicle (EEV)-Conjugated Phosphorodiamidate Morpholino Oligomer (PMO) Therapeutics for the Treatment of Duchenne Muscular Dystrophy
Time: 4:45 pm
day: Day One
Details:
- Understanding endosomal escape vehicle platform – an enhance lipid nanoparticlemediated delivery of genomic medicines
- Considering the value proposition of using endosomal escape vehicle-oligonucleotides for Duchenne
- Analyzing preclinical data to support this novel approach
